UNIMAB Project by Giulio Cossu

Towards a new cell therapy for muscular dystrophy Muscular dystrophies are heterogeneous diseases, characterized by primary wasting of skeletal muscle. Duchenne Muscular Dystrophy (DMD) is the most common muscular dystrophy and the second most common monogenic disorder, affecting 1/5000 newborn males.  DMD is a severe disease, leading to wheelchair dependency, cardiac and respiratory failure, and…